Mom Finds Experimental Drug for Twins’ Fatal Cholesterol Condition; FDA Approves Treatment Under Compassionate Use Program

Good Morning America reports on the Food and Drug Administration’s approval of Addi and Cassi’s compassionate use Investigational New Drug Application to give them intravenous infusions of cyclodextrin, a non toxic sugar compound found in everyday food products. Cyclodextrin may have the ability to remove trapped cellular cholesterol from Addi and Cassi’s brain, liver and […]

Good Morning America Features Addi and Cassi’s Fight Against Fatal Brain Disease

On May 1st, 2008, Addi and Cassi’s fight against Niemann Pick Type C was featured on ABC News Good Morning America. Please spend a few minutes to read the entire story and watch the 4 minute segment.  We are very grateful to Good Morning America for taking the time to create this thoughtful and caring […]