Wednesday, September 27, 2023

New FDA ‘Rare Disease’ Division Being Proposed to U.S. House Committee on Appropriations

May 22, 2010 by  
Filed under Featured Stories

The Kakkis Every Life Foundation is leading the effort to request $10 million in the fiscal year 2011 Ag-Rural Development-FDA Appropriations bill directing the U.S. Food and Drug Administration to establish a new review division for Biochemical and Genetic Diseases within the Center for Drug Evaluation Research (CDER), Office of New Drugs. A letter from […]

World Rare Disease Day 2009 Genes Video

February 2, 2009 by  
Filed under Rare Disease, Videos

I made this video for World Rare Disease Day 2008 to bring global attention to the fact that Rare Disease is not so rare — it can happen to anyone or any family. Although each Rare Disease affects a small number of people, taken all together rare diseases affect millions of people in the world. […]