FDA Filing Made Requesting Use of Medtronic SynchroMed Pump To Deliver Cyclodextrin To Brain
April 13, 2011 by Chris Hempel
Filed under Featured Stories
To say I am pumped up today is an understatement! We’ve reached another historic milestone in our effort to treat Addi and Cassi with cyclodextrin! Dr. Caroline Hastings at Children’s Hospital Research Center Oakland filed a 400+ page document with the FDA yesterday on behalf of the twins seeking a permanent solution to deliver hydroxyl-propyl-beta-cyclodextrin […]
Insulin Therapy and Alzheimer’s – Could Cyclodextrin Sugar Act on Insulin and Glucose Metabolism?
April 10, 2011 by Chris Hempel
Filed under Uncategorized
Recently reports in the news shows how insulin therapy may be a treatment for Alzheimer’s. Basically, a low dose of insulin has been found to suppress the expression in the blood of four precursor proteins involved in the pathogenesis of Alzheimer’s disease, according to research by University at Buffalo endocrinologists. Paresh Dandona, MD, PhD, University […]
Rare Disease Foundations Need To Vote 4 Hope In Pepsi Refresh
September 1, 2010 by Chris Hempel
Filed under Videos
During the Vote4Hope Pepsi Refresh Rare Disease Campaign, I am making video postings on Addi and Cassi’s website to raise awareness for all rare diseases, not just the horrific disease called Niemann Pick Type C that I am fighting against on behalf of my six year old identical twins. Please take a minute to watch […]
FDA Does Not Approve Actelion’s Zavesca in US – Distressing News For Niemann Pick Type C Community
March 9, 2010 by Chris Hempel
Filed under Featured Stories
Actelion, the makers of Zavesca, today put out a brief statement saying that the U.S. Food and Drug Administration did not approve Zavesca and wants more information from the company on treating Niemann Pick Type C, a rare and dementing neurological disease that afflicts our six year old identical twins, Addi and Cassi. Niemann Pick Type C disease is caused […]
The Road to Building a New Orphan Drug – Am I Mad?
February 4, 2010 by Chris Hempel
Filed under Cyclodextrin
On February 25-26, 2010, I will be attending the inaugural FDA Build-an-Orphan-Drug-Workshop hosted by the Center for Rare Disease Therapies at Keck Graduate Institute (KGI) in Claremont, Calif. FDA agency experts will be on hand to provide guidance on applying for orphan drug designation. I will be attending the workshop with Dr. Ron Browne, hired […]