Extraordinary Measures Movie Is A National Healthcare Wake Up Call
January 13, 2010 by Chris Hempel
Filed under Featured Stories
Extraordinary Measures, a new movie centered on the efforts of John and Aileen Crowley to find a researcher who might help find a cure for their two children’s rare genetic disease (Pompe Disease), will hit theaters on January 22. I can’t wait to see this movie! The trailer sounds eerily familiar as we are working around […]
How Cyclodextrin Solution Is Made For Addi and Cassi’s Intravenous Cyclodextrin Therapy
November 25, 2009 by Chris Hempel
Filed under Cyclodextrin
A number of people from around the world who have children diagnosed with the fatal cholesterol disease called Niemann Pick Type C have asked me how our we prepare our cyclodextrin solution for Addi and Cassi’s bi-weekly IV infusions of the compound. All hydroxy propel beta cyclodextrin (HPBCD) is not the same. It’s very important […]
Nobel Prize Winning Cholesterol Researchers Brown and Goldstein Enter Cyclodextrin Field Of Study
November 10, 2009 by Chris Hempel
Filed under Featured Stories
I wonder how many smart cholesterol researchers have Google Alerts set up on Brown and Goldstein Labs? If they do they might want to read this post about the Nobel Prize winning labs release of a very important cholesterol paper involving cyclodextrin and its modulation of cellular cholesterol metabolism. With their amazing new research work, […]
Parents To Seek FDA Orphan Drug Designation For Cyclodextrin To Treat Rare and Fatal Cholesterol Disease
October 10, 2009 by Chris Hempel
Filed under Cyclodextrin, Cyclodextrin News
On Tuesday morning at 11am, Addi and Cassi are going to undergo volumetric CT scans of their livers and spleens. The tests are being conducted by doctors to determine if the cyclodextrin IV infusion treatment the twins are receiving under compassionate use INDs approved by the FDA are reducing the size of their enlarged cholesterol […]
FDA Investigational New Drug Application Documents for Cyclodextrin Treatment for Niemann Pick Type C Disease
September 13, 2009 by Chris Hempel
Filed under FDA Cyclodextrin Filings
Here you will find detailed documents outlining Addi and Cassi’s cyclodextrin infusion treatments. We filed a compassionate use IND application to the US FDA in early 2009 to give intravenous cyclodextrin treatment which was approved. In September 2010, FDA approved a new request to put HPBCD directly into the brains of the twins. Addi and […]
