FDAs Orphan Drug Workshop Featured in Wall Street Journal – Push To Cure Rare Diseases

Below is a story that ran in today’s Wall Street Journal (Page A 3) on the FDA workshop I attended a few week ago at the Keck Graduate Institute in Claremont, CA.  We filed an orphan drug application for Cyclodextrin for the treatment of Niemann Pick Type C disease, an ultra rare cholesterol disease that […]

I am Green Beans and Ensure!

I am laughter until my belly hurts. I am strong, plus I have muscles. I am Illinois and Iowa. I am a brother with many parents. I am a sports fan. I am dogs and cats, horses and cows fan. I am green beans and Ensure. I am Happy Joe’s on a Friday night. I […]

Obama Cracks Jokes About Cholesterol Level And Personal Health – Is He Out of Touch?

I almost had a heart attack today (no pun intended) when I read that President Obama was joking about his cholesterol.  “I don’t want any lectures about my cholesterol,” he said, according to the pool report. If President Obama needs inspiration to cut his cholesterol and push away that fried chicken the next time he […]

Numbers Don’t Add Up – Only 347 New Drugs Approved By FDA For 30 Million Americans With Rare Disease in Past 25 Years?

When it comes to finding Rare Disease statistics, the same old statistics and facts keep popping up again and again. I realize data is difficult to gather on 7000 different rare diseases that afflict 30 million Americans but it’s frustrating that sports teams and Wall Street have more comprehensive statistics when millions of people across […]

Stem Cells For Dummies: The Controvery, Pros and Cons, Facts, Future Research

Ok, I admit it. I am a Dummie!  Especially when it comes to Science!  I do hold a Bachelor of Arts in Political Science from Berkeley but it’s not exactly the type of “Science” degree you need when your children are dying from a rare cholesterol disease that causes dementia. All of a sudden topics […]

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