Wednesday, May 27, 2020

FDAs Orphan Drug Workshop Featured in Wall Street Journal – Push To Cure Rare Diseases

March 10, 2010 by  
Filed under Featured Stories

Below is a story that ran in today’s Wall Street Journal (Page A 3) on the FDA workshop I attended a few week ago at the Keck Graduate Institute in Claremont, CA.  We filed an orphan drug application for Cyclodextrin for the treatment of Niemann Pick Type C disease, an ultra rare cholesterol disease that […]